Advocacy Groups Join Reagan-Udall Foundation and FDA for Workshop on Developing Biomarkers to Support Accelerated Approval in Rare Diseases
Workshop Presented Overwhelming Scientific Evidence to Support CSF-HS as a Primary Biomarker in Neuropathic MPS Disorders On February 21, 2024, Cure Sanfilippo Foundation, National MPS...
The Assistance Fund Opens New Program for Systemic Sclerosis
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With Systemic Sclerosis The Assistance Fund, an independent charitable patient assistance organization that...
The Assistance Fund Opens New Program for Neurofibromatosis
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With Neurofibromatosis The Assistance Fund, an independent charitable patient assistance organization that helps...
CMTA Appoints Biotech Industry Veteran Suzanne Bruhn, PhD as New CEO
The Charcot-Marie-Tooth Association announced Nov. 6 that Suzanne (Sue) Bruhn, PhD, an accomplished biotech executive with extensive experience in the development and commercialization of treatments...
The Assistance Fund Opens New Program for Epidermolysis Bullosa
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With Epidermolysis Bullosa The Assistance Fund, an independent charitable patient assistance organization that...
The Assistance Fund Opens New Program for Idiopathic Hypersomnia
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With Idiopathic Hypersomnia The Assistance Fund, an independent charitable patient assistance organization that...
The Assistance Fund Opens New Program for Activated Phosphoinositide 3-Kinase Delta Syndrome (APDS)
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With APDS The Assistance Fund, an independent charitable patient assistance organization that helps...
The Assistance Fund Appoints Danielle Vizcaino as Its New President and Chief Executive Officer
The Assistance Fund (TAF), an independent, charitable patient assistance organization that helps patients and families facing high medical out-of-pocket costs, today announced that its Board...
Ambit Hires Jonathan Woodring as Chief Innovation Officer
Former IPM.ai executive to drive data and analytics product strategy, development, and commercialization. Ambit, a leading biopharma solutions company, has announced the hiring of Jonathan...
The Assistance Fund Opens New Program for Rett Syndrome
Financial Assistance From The Assistance Fund Now Available for Eligible People Living With Rett Syndrome The Assistance Fund, an independent charitable patient assistance organization that...